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Zolgensma

/zoʊlgˈzæmənz/ /zəlˈdʒɛnsmə/
noun
GeneralMedical
  1. 1 Zolgensma
  2. 2 nadir görülen genetik bir sinir-kas hastalığı için tek seferlik tedavi

Definition (English)

  1. A gene therapy drug used to treat spinal muscular atrophy (SMA) in infants and children.
  2. It is a one-time treatment for a rare genetic neuromuscular disorder.

Example Sentences

  1. Zolgensma is a groundbreaking treatment.
    Zolgensma çığır açan bir tedavidir.
  2. The baby received Zolgensma.
    Bebek Zolgensma aldı.

Collocations

zolgensma treatmentzolgensma therapyzolgensma drugzolgensma administrationzolgensma approvalzolgensma cost